Dysferlin deficiency causes two forms of muscular dystrophy: Miyoshi distal myopathy and Limb-Girdle Muscular dystrophy type 2B. The dysferlin gene and protein were discovered in 1998; many research groups around the world are currently studying this medical condition. This group is intended to give patients, families, researchers, and others the opportunity to share information, experiences, and advice.
to my understanding (no scientist here), the delivery method is different for different versions of the the follistatin gene. i rather use the soluble fusion
Hi Matt, Thank you for the link to Acceleron. Looks promising, but it is a totally different compound than the Myo-29 study that was conducted by Wyeth, which
hey Josh. dont now if you know that accelleron already compleeted phase 1 study for the same or maybe beefed up compounds, as the mda grantees do. that's in
A brief description on myostatin, etc. to try to make the discussion understandable to everyone. Myostatin is a protein that is a negative regulator of muscle
Matt, Thank you for the Science Daily link. That is very interesting and encouraging in my opinion. Could you explain why you consider what Dr. Mendell is